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Article

Novel genetic therapeutic approaches for modulating the severity of β‑thalassemia (Review)

2 Sept 2020

Abstract excerpt

Thalassemia is a genetic haematological disorder that arises due to defects in the α and β‑globin genes. Worldwide, 0.3‑0.4 million children are born with haemoglobinopathies per year. Thalassemic patients, as well as their families, face various serious clinical, socio‑economic, and psychosocial challenges throughout their life. Different therapies are available in clinical practice to minimize the suffering of...

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PMID: 32953110
DOI: 10.3892/br.2020.1355

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