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Article

Prospects for retinal gene replacement therapy.

Trends in genetics : TIG - 1 Apr 2009

Smith Alexander J, Bainbridge James W, Ali Robin R

Abstract excerpt

Inherited retinal degeneration, which includes conditions such as retinitis pigmentosa and Leber congenital amaurosis (LCA), affects approximately 1/3000 of the population in the Western world. It is characterized by loss of vision and results from mutations in any one of >100 different genes. There are currently no effective treatments, but many of the genes have now been identified and their functions...

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Source

Identifiers

PMID: 19303164
DOI: 10.1016/j.tig.2009.02.003

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-07.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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