Article
Revolution in Gene Medicine Therapy and Genome Therapy
2018-10-01
Abstract excerpt
Recently, there have been revolutions in the development of both gene therapy and genome surgical treatments for inherited diseases. Much of this progress has been centered around hereditary retinal dystrophies, because the eye is an immune-privileged and anatomically ideal target. Gene therapy treatments, already demonstrated to be safe and efficacious in numerous clinical trials, are benefitting from the develop...
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Identifiers and source
- Literature Corpus work
- f995846a-e583-55ba-b552-11444048ae30
- DOI
- 10.20944/preprints201810.0010.v1