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Exploring Barriers to Clinical Trial Readiness Among the Myotonic Dystrophy Community: A Mixed-Methods Study

2026-03-13

Abstract excerpt

<title>Abstract</title> <p>Myotonic dystrophy (DM) is a multisystemic disorder characterized by significant heterogeneity in symptom manifestation, progression, and severity. This variability complicates clinical trial design and implementation, thereby affecting therapeutic development. This study aimed to identify barriers to clinical trial readiness in DM and explore actionable solutions by incorporating persp...

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Literature Corpus work
f4cf119e-17a1-5eb4-a679-338609c104d0
DOI
10.21203/rs.3.rs-8961613/v1
Open publication

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Exploring Barriers to Clinical Trial Readiness Among the Myotonic Dystrophy Community: A Mixed-Methods StudyDOI 10.21203/rs.3.rs-8961613/v1
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