Back to search

Article

Gene Therapy: A Revolutionary Step in Treating Thalassemia

2024-06-03

Abstract excerpt

Beta thalassemia is an inherited blood disorder that results in inefficient erythropoiesis due to genetic mutation that leads to reduction or absence of the hemoglobin beta-globulin protein. Approximately 8.5% of UAE residents suffer from β-thalassemia, a significant health and financial problem. The treatment options available for β-Thalassemia major are limited and associated with a wide range of complications....

Topics

Open a Topic to create a Post that cites this publication.

Identifiers and source

Literature Corpus work
ca8fa3cb-2591-5dcc-bde3-a1354268025a
DOI
10.20944/preprints202406.0024.v1
Open publication

Related research

Semantic proximity does not establish scientific evidence.

Click a neighbor to travelStep 1 · 12 closest
Interactive article relationship graphSelect a related publication card to move it into the centre and load its closest explainable connections. Solid lines are source-backed structured connections. Dashed lines are semantic discovery signals and are not scientific evidence.
Gene Therapy: A Revolutionary Step in Treating ThalassemiaDOI 10.20944/preprints202406.0024.v1
Gene Therapy: A Revolutionary Step in Treating ThalassemiaSemantic proximity
Gene Therapy for β-Hemoglobinopathies: From Discovery to Clinical TrialsSemantic proximity
The potential of gene therapy approaches for the treatment of hemoglobinopathies: achievements and challengesSemantic proximity
Recent advancements in gene therapy for sickle cell disease and β-thalassemiaSemantic proximity
Gene therapies for transfusion dependent β‐thalassemia: Current status and critical criteria for successSemantic proximity
Gene Addition Strategies for β-Thalassemia and Sickle Cell Anemia.Semantic proximity
Gene Therapy for β-Haemoglobinopathies: From Molecular Correction to Curative MedicineSemantic proximity
Hurdles to the Adoption of Gene Therapy as a Curative Option for Transfusion-Dependent ThalassemiaSemantic proximity
Gene Therapy for HemoglobinopathiesSemantic proximity
Gene Therapy for Beta-Hemoglobinopathies: Milestones, New Therapies and ChallengesSemantic proximity
Gene therapy in transfusion-dependent non-β0/β0 genotype β-thalassemia: first real-world experience of beti-cel.Semantic proximity
Recent trends in the gene therapy of β-thalassemiaSemantic proximity
Select a neighboring publication to make it the new centre.