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Gene Therapy: A Revolutionary Step in Treating Thalassemia

21 Oct 2024

Abstract excerpt

Beta thalassemia is an inherited blood disorder that results in inefficient erythropoiesis due to genetic mutation that leads to the reduction or absence of the hemoglobin beta-globulin protein. Approximately 8.5% of UAE residents suffer from β-thalassemia, a significant health and financial problem. The treatment options available for β-Thalassemia major are limited and associated with a wide range of...

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PMID: 39449307
DOI: 10.3390/hematolrep16040064

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