Article

Special Issue: Neuromuscular Cardiopulmonary Medicine in the Age of Emerging Therapies

2020-11-09

Abstract excerpt

Neuromuscular medicine is being revolutionized by new genetic and molecular therapies. The purpose of this Special Issue is to present an overview of these new therapies, to examine their cardiopulmonary effects, and to consider the future of neuromuscular cardiopulmonary care. The emphasis will be on Duchenne muscular dystrophy (DMD) and, to a lesser extent, spinal muscular atrophy (SMA), as these are the disease...

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Literature Corpus work: b836d819-08cd-588f-b481-414c4283baa3
DOI: 10.22541/au.160490709.98314090/v1

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