Article

The Burden of Illness in Patients with Familial Chylomicronemia Syndrome (FCS) in the United Kingdom

2019-09-11

Abstract excerpt

<title>Abstract</title> <p>Background: Familial chylomicronemia syndrome (FCS) is a rare genetic disorder associated with a deficiency in lipoprotein lipase activity, which is characterized by severe hypertriglyceridemia, recurrent abdominal pain and episodes of acute pancreatitis. Investigation of Findings and Observations Captured in Burden of Illness Survey in FCS Patients (IN-FOCUS) assessed the impact of FCS...

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Literature Corpus work: a3b9c492-55b4-5f20-9f34-303bf1a6c863
DOI: 10.21203/rs.2.14290/v1

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