Article

On the in vivo kinetics of gene delivery vectors

2022-02-14

Abstract excerpt

Gene therapy is the most promising strategy for treating a number of diseases at their most fundamental, genetic level, and it has a wide range of promising clinical and emerging preclinical uses in both the clinic and the laboratory. Gene therapy systems are composed of three fundamental components, with the delivery platform being responsible for the protection and successful delivery of the incorporated therape...

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Literature Corpus work: a3b52434-42cb-574c-a747-7f80120ee2f2
DOI: 10.1101/2022.02.11.22269834

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