Back to search

Article

CRISPR-Cas9 Gene Therapy Effects on Inherited Eye Disorders

2025-06-02

Abstract excerpt

Abstract Stargardt’s Disease (STGD1), Retinitis pigmentosa (RP), and Leber’s congenital amaurosis (LCA) inherited eye conditions that are among the main causes of blindness and visual impairment. The primary cause of these diseases, which lead to gradual vision loss, is genetic mutations affecting retinal cells. Gene-editing technologies, especially the CRISPR-Cas9 system, are emerging as promising way...

Topics

Open a Topic to create a Post that cites this publication.

Identifiers and source

Literature Corpus work
9b52f9dc-6f43-5ece-94f9-dd1f2ec7c30c
DOI
10.20944/preprints202506.0093.v1
Open publication

Related research

Semantic proximity does not establish scientific evidence.

Click a neighbor to travelStep 1 · 12 closest
Interactive article relationship graphSelect a related publication card to move it into the centre and load its closest explainable connections. Solid lines are source-backed structured connections. Dashed lines are semantic discovery signals and are not scientific evidence.
CRISPR-Cas9 Gene Therapy Effects on Inherited Eye DisordersDOI 10.20944/preprints202506.0093.v1
CRISPR Interference-Potential Application in Retinal Disease.Semantic proximity
CRISPR-Based Genome Editing as a New Therapeutic Tool in Retinal Diseases.Semantic proximity
From bench to bedside: Developing CRISPR/Cas-based therapy for ocular diseasesSemantic proximity
Rescue of the disease-associated phenotype in CRISPR-corrected hiPSCs as a therapeutic approach for inherited retinal dystrophiesSemantic proximity
Therapeutic applications of CRISPR /Cas9 gene editing technology for the treatment of ocular diseasesSemantic proximity
Genome-Editing Strategies for Treating Human Retinal DegenerationsSemantic proximity
The Application of CRISPR/Cas9 for the Treatment of Retinal Diseases.Semantic proximity
The application and progression of CRISPR/Cas9 technology in ophthalmological diseasesSemantic proximity
Using CRISPR-Cas9 to Generate Gene-Corrected Autologous iPSCs for the Treatment of Inherited Retinal Degeneration.Semantic proximity
Emerging Therapeutic Approaches and Genetic Insights in Stargardt Disease: A Comprehensive Review.Semantic proximity
Gene therapy for inherited retinal diseases: exploiting new tools in genome editing and nanotechnologySemantic proximity
Precision genome editing in the eye.Semantic proximity
Select a neighboring publication to make it the new centre.