Article

Assessment of motor function and nutritional status in children with spinal muscular atrophy treated with nusinersen after loading period in western China

2022-09-02

Abstract excerpt

<h4>Introduction: </h4> The treatment of children with spinal muscular atrophy (SMA) includes disease-modifying drugs such as nusinersen. Our aim was to summarize our experience regarding the efficacy and safety of nusinersen and nutritional status in children with SMA in western China. <h4>Methods:</h4> In this retrospective study, data from all patients with a genetically confirmed diagnosis of SMA before 18 yea...

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Literature Corpus work: 87d89418-39e9-519d-bf4c-2e022d9da6a4
DOI: 10.21203/rs.3.rs-1914460/v1

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