In Vivo Gene Editing: A Healthcare Revolution in the Making

Abstract excerpt

Gene or genome editing (GE) revises, removes, or replaces a mutated gene at the DNA level; it is a tool. Gene therapy (GT) offsets mutations by introducing a "normal" version of the gene into the body while the diseased gene remains in the genome; it is a medicine. So far, no in vivo GE product has been approved, as opposed to 22 GT products approved by the FDA. However, several are under development, an...

Topics

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• CRISPR and Genetic Engineering
• CRISPR-Cas Systems
• Gene Editing
• Gene Transfer Techniques
• Germ Cells
• Mutation
• Precision Medicine
• Virus-based gene therapy research

Identifiers and source

Literature Corpus work

4a8c37fd-b4c8-5855-889c-e5cc40d98be1

DOI

10.20944/preprints202308.0453.v1