Discover Community Create You

Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Site-specific genome editing in treatment of inherited diseases: possibility, progress, and perspectives

1 Oct 2022

Abstract excerpt

Abstract Advancements in genome editing enable permanent changes of DNA sequences in a site-specific manner, providing promising approaches for treating human genetic disorders caused by gene mutations. Recently, genome editing has been applied and achieved significant progress in treating inherited genetic disorders that remain incurable by conventional therapy. Here, we present a review of various programmable...

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to CRISPR and Genetic Engineering
Share to Mosquito-borne diseases and control
Share to RNA regulation and disease

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Source

Identifiers

PMID: 37724161
DOI: 10.1515/mr-2022-0029

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 8 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Site-specific genome editing in treatment of inherited diseases: possibility, progress, and perspectivesPMID 37724161Read ↗

Current landscape of gene‐editing technology in biomedicine: Applications, advantages, challenges, and perspectivesSemantic proximity Read ↗

The history, use, and challenges of therapeutic somatic cell and germline gene editing.Semantic proximity Read ↗

Advances in genome editing: the technology of choice for precise and efficient β-thalassemia treatmentSemantic proximity Read ↗

Building Gene Editing Platforms for Personalized Medicine: The Next Step in Interventional GeneticsSemantic proximity Read ↗

Advancing Precision Medicine: Recent Innovations in Gene Editing TechnologiesSemantic proximity Read ↗

Editing outside the body: Ex vivo gene-modification for β-hemoglobinopathy cellular therapy.Semantic proximity Read ↗

Prime editing: A gene precision editing tool from inception to present.Semantic proximity Read ↗

Breaking genetic shackles: The advance of base editing in genetic disorder treatmentSemantic proximity Read ↗

Prime Editing for Human Gene Therapy: Where Are We Now?Semantic proximity Read ↗

Gene and cell therapy of human genetic diseases: Recent advances and future directionsSemantic proximity Read ↗

Base Editing and Prime Editing: Potential Therapeutic Options for Rare and Common Diseases.Semantic proximity Read ↗

ASGCT and JSGT Joint Position Statement on Human Genomic EditingSemantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.