Article

Fanconi Anemia: Hematopoietic Stem Cell Transplant or Gene Therapy?

2021-12-15

Abstract excerpt

FA is a rare, multi-organ cancer-prone IBMFS associated with hematological malignancies and STs. The androgen therapy, hematopoietic growth factors, HSCT, and GT, still in the clinical trial, are various treatments for this disease. Here, we aimed to compare the advantages and disadvantages of HSCT and GT in FA cures. We perform an advanced electronic search of “FA” AND (genetics OR treatment OR HSCT OR GT OR Mosa...

Topics

Open a Topic to create a Post that cites this publication.

Identifiers and source

Literature Corpus work: 488ef277-b7c4-5a3e-8260-fa9adaa51246
DOI: 10.22541/au.163907554.49456927/v2

Open publication

Related research

Semantic proximity does not establish scientific evidence.

Click a neighbor to travelStep 1 · 12 closest

Fanconi Anemia: Hematopoietic Stem Cell Transplant or Gene Therapy?DOI 10.22541/au.163907554.49456927/v2Read

How I manage patients with Fanconi anaemia.Semantic proximity Read

How I treat MDS and AML in Fanconi anemiaSemantic proximity Read

Special pre- and posttransplant considerations in inherited bone marrow failure and hematopoietic malignancy predisposition syndromesSemantic proximity Read

Somatic, hematologic phenotype, long-term outcome, and effect of hematopoietic stem cell transplantation. An analysis of 97 Fanconi anemia patients from the Italian national database on behalf of the Marrow Failure Study Group of the AIEOP (Italian Association of Pediatric Hematology-Oncology).Semantic proximity Read

Investigation of mutations in Fanconi anemia genes and malignancy predisposition in Brazilian patients.Semantic proximity Read

Hematopoietic stem cell transplantation for classical inherited bone marrow failure syndromes: an updateSemantic proximity Read

Fanconi AnemiaSemantic proximity Read

Haplo‐identical or mismatched unrelated donor hematopoietic cell transplantation for Fanconi anemia: Results from the Severe Aplastic Anemia Working Party of the EBMTSemantic proximity Read

Alternative donor hematopoietic cell transplantation for Fanconi anemiaSemantic proximity Read

[Fanconi anemia in 2012: diagnosis, pediatric follow-up and treatment].Semantic proximity Read

Phenotypes of adults with Fanconi anaemia.Semantic proximity Read

Benign Tumors and Non-Melanoma Skin Cancers in Patients with Fanconi AnemiaSemantic proximity Read