Article

The STArgardt Remofuscin Treatment Trial (STARTT): design and baseline characteristics of enrolled Stargardt patients

2022-09-27

Abstract excerpt

<h4>Background: </h4> This report describes the study design and baseline characteristics of patients with Stargardt disease (STGD1) enrolled in the STArgardt Remofuscin Treatment Trial (STARTT). <h4>Methods: </h4>: In total, 87 patients with genetically confirmed STGD1 were randomized in a double-masked, placebo-controlled proof of concept trial to evaluate the safety and efficacy of 20 milligram oral remofuscin...

Topics

Open a Topic to create a Post that cites this publication.

Identifiers and source

Literature Corpus work: 3d4ac799-f42d-5e24-a0d2-c5d4c1f52426
DOI: 10.12688/openreseurope.13872.3

Open publication

Related research

Semantic proximity does not establish scientific evidence.

Click a neighbor to travelStep 1 · 12 closest

The STArgardt Remofuscin Treatment Trial (STARTT): design and baseline characteristics of enrolled Stargardt patientsDOI 10.12688/openreseurope.13872.3Read

The Natural History of the Progression of Atrophy Secondary to Stargardt Disease (ProgStar) Studies: Design and Baseline Characteristics: ProgStar Report No. 1.Semantic proximity Read

Stargardt macular dystrophy and therapeutic approaches.Semantic proximity Read

Study of Late-Onset Stargardt Type 1 DiseaseSemantic proximity Read

Stargardt disease: clinical features, molecular genetics, animal models and therapeutic options.Semantic proximity Read

Foveal sparing in Stargardt disease.Semantic proximity Read

Stargardt-Fundus Flavimaculatus: Recent Advancements and TreatmentSemantic proximity Read

Stargardt disease and progress in therapeutic strategies.Semantic proximity Read

Test–Retest Variability of Functional and Structural Parameters in Patients with Stargardt Disease Participating in the SAR422459 Gene Therapy TrialSemantic proximity Read

Visual Acuity Change Over 24 Months and Its Association With Foveal Phenotype and Genotype in Individuals With Stargardt Disease: ProgStar Study Report No. 10.Semantic proximity Read

Stargardt macular dystrophy and evolving therapiesSemantic proximity Read

The ABCs of Stargardt disease: the latest advances in precision medicineSemantic proximity Read

New insights into Stargardt disease with multimodal imaging.Semantic proximity Read