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Article

Problems and potential for gene therapy in Duchenne muscular dystrophy.

Neuromuscular disorders : NMD - 1 Jul 1997

Kakulas B A

Abstract excerpt

Hopes ran high that a cure for Duchenne muscular dystrophy (DMD) would quickly follow the discovery of dystrophin by Lou Kunkel and his group in the 1980's. Myoblast transplantation, the favoured method of gene 'complementation', unfortunately did not progress beyond the experimental stage. A more sober approach to gene therapy followed using a variety of transfection or direct methods to introduce the normal...

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Source

Identifiers

PMID: 9267845
DOI: 10.1016/s0960-8966(97)00056-4

Genes

DMD

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-08.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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Lack of mRNA and dystrophin expression in DMD patients three months after myoblast transferSemantic proximity Read ↗

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