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Article

Challenges for gene therapy for muscular dystrophy.

Current neurology and neuroscience reports - 1 Jan 2006

Mendell Jerry R, Clark K Reed

Abstract excerpt

Gene therapy for muscular dystrophy represents a promising avenue of pursuit for a disease with a limited repertoire of treatment. Recent successes in the research arena using adeno-associated viral vectors should accelerate the movement of gene-based therapeutics for muscle disorders into the cl...

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Identifiers

PMID: 16469271
DOI: 10.1007/s11910-996-0009-8

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 2 Sept 2026. Prepared record publication-16469271-2026-09-02.1. Manifest publication-graph-cohort-2026-09-02.1.

Source receipt: PubMed via Helena Literature Corpus, retrieved 2 Sept 2026.

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