Article
Clinical Characteristics of Cryopyrin-Associated Periodic Syndrome and Long-Term Real-World Efficacy and Tolerability of Canakinumab in Japan: Results of a Nationwide Survey.
Arthritis & rheumatology (Hoboken, N.J.) - 1 Jun 2024
Miyamoto Takayuki, Izawa Kazushi, Masui Sho, Yamazaki Atsue, Yamasaki Yuichi, Matsubayashi Tadashi, Shiraki Mayuka, Ohnishi Hidenori, Yasumura Junko, Kawabe Tomohiro, Miyamae Takako, Matsubara Tomoyo, Arakawa Naoya, Ishige Takashi, Takizawa Takumi, Shimbo Asami, Shimizu Masaki, Kimura Naoki, Maeda Yuichi, Maruyama Yuta, Shigemura Tomonari, Furuta Junichi, Sato Satoshi, Tanaka Hiroshi, Izumikawa Miharu, Yamamura Masahiro, Hasegawa Toshio, Kaneko Hiroshi, Nakagishi Yasuo, Nakano Naoko, Iida Yasunori, Nakamura Tamaki, Wakiguchi Hiroyuki, Hoshina Takayuki, Kawai Toshinao, Murakami Kosaku, Akizuki Shuji, Morinobu Akio, Ohmura Koichiro, Eguchi Katsuhide, Sonoda Motoshi, Ishimura Masataka, Furuno Kenji, Kashiwado Momoko, Mori Masaaki, Kawahata Kimito, Hayama Koremasa, Shimoyama Kumiko, Sasaki Natsuko, Ito Taisuke, Umebayashi Hiroaki, Omori Tae, Nakamichi Seiko, Dohmoto Tomotsune, Hasegawa Yasuyuki, Kawashima Hisashi, Watanabe Shojiro, Taguchi Yuichiro, Nakaseko Haruna, Iwata Naomi, Kohno Hiroki, Ando Taiki, Ito Yasuhiko, Kataoka Yuko, Saeki Takako, Kaneko Utako, Murase Ayako, Hattori Seira, Nozawa Tomo, Nishimura Kenichi, Nakano Reiji, Watanabe Misa, Yashiro Masato, Nakamura Tomonori, Komai Toshihiko, Kato Kentaro, Honda Yoshitaka, Hiejima Eitaro, Yonezawa Atsushi, Bessho Kazuhisa, Okada Satoshi, Ohara Osamu, Takita Junko, Yasumi Takahiro, Nishikomori Ryuta
Abstract excerpt
OBJECTIVE: We assess the clinical characteristics of patients with cryopyrin-associated periodic syndrome (CAPS) in Japan and evaluate the real-world efficacy and safety of interleukin-1 (IL-1) inhibitors, primarily canakinumab. METHODS: Clinical information was collected retrospectively, and serum concentrations of canakinumab and cytokines were analyzed. RESULTS: A total of 101 patients were included, with 86...
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