CFTR modulator therapy: transforming the landscape of clinical care in cystic fibrosis.

Abstract excerpt

Following discovery of the cystic fibrosis transmembrane conductance regulator (CFTR) gene in 1989 and subsequent elucidation of the varied CFTR protein abnormalities that result, a new era of cystic fibrosis management has emerged-one in which scientific principles translated from the bench to the bedside have enabled us to potentially treat the basic defect in the majority of children and adults with cystic...

Topics

Share this publication in a Topic to start or enrich a Post.

• Share to Aminophenols
• Share to Child
• Share to Cystic Fibrosis