Article
Rare bleeding disorders and advances in gene therapy.
Blood coagulation & fibrinolysis : an international journal in haemostasis and thrombosis - 1 Dec 2019
Liu Tian, Yang Zhigang
Abstract excerpt
: Rare bleeding disorders usually begin in childhood and manifest as varying degrees of bleeding, which can be life-threatening in severe cases. With the development of gene editing technology, it is expected that hereditary coagulation factor disorders will someday be fundamentally cured by gene therapy. On account of their rarity, comprehension of these diseases is essential for the application of new treatment...
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