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Generation of two compound heterozygous HGSNAT-mutated lines from healthy induced pluripotent stem cells using CRISPR/Cas9 to model Sanfilippo C syndrome.

Stem cell research - 1 Dec 2019

Benetó Noelia, Cozar Monica, García-Morant María, Creus-Bachiller Edgar, Vilageliu Lluïsa, Grinberg Daniel, Canals Isaac

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Methodology Data sources Editorial policy Privacy Delete account & data About Contact Helena Bioinformatics

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PMID: 31731183
DOI: 10.1016/j.scr.2019.101616

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