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Article

Complete correction of hemophilia B phenotype by FIX-Padua skeletal muscle gene therapy in an inhibitor-prone dog model.

Blood advances - 13 Mar 2018

French Robert A, Samelson-Jones Benjamin J, Niemeyer Glenn P, Lothrop Clinton D, Merricks Elizabeth P, Nichols Timothy C, Arruda Valder R

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Share to Dependovirus
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Share to Genetic Therapy

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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Identifiers

PMID: 29500218
DOI: 10.1182/bloodadvances.2017015313
PMCID: PMC5851422

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