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Article

New treatments targeting the basic defects in cystic fibrosis.

Presse medicale (Paris, France : 1983) - 1 Jun 2017

Fajac Isabelle, Wainwright Claire E

Abstract excerpt

Cystic fibrosis (CF) is a monogenic autosomal recessive disorder affecting around 75,000 individuals worldwide. It is a multi-system disease but the main morbidity and mortality is caused by chronic lung disease. Due to newborn screening, a multidisciplinary approach to care and intensive symptomatic treatment, the prognosis has dramatically improved over the last decades and there are currently more adults than...

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Identifiers

PMID: 28554723
DOI: 10.1016/j.lpm.2017.01.024

Genes

CFTR

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-08.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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