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Article

Repeated administrations of human umbilical cord blood cells improve disease outcomes in a mouse model of Sanfilippo syndrome type III B.

Cell transplantation - 1 Jan 2014

Willing Alison E, Garbuzova-Davis Svitlana N, Zayko Olga, Derasari Hiranya M, Rawls Ashley E, James Chris R, Mervis Ron F, Sanberg Cyndy D, Kuzmin-Nichols Nicole, Sanberg Paul R

Abstract excerpt

Sanfilippo syndrome type III B (MPS III B) is an inherited disorder characterized by a deficiency of α-N-acetylglucosaminidase (Naglu) enzyme leading to accumulation of heparan sulfate in lysosomes and severe neurological deficits. We have previously shown that a single administration of human um...

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Identifiers

PMID: 25565636
DOI: 10.3727/096368914X676916

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 4 Sept 2026. Prepared record publication-25565636-2026-09-04.2. Manifest publication-graph-cohort-2026-09-04.2.

Source receipt: PubMed via Helena Literature Corpus, retrieved 4 Sept 2026.

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Repeated administrations of human umbilical cord blood cells improve disease outcomes in a mouse model of Sanfilippo syndrome type III B.PMID 25565636Read ↗

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