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Article

Gene-based therapies for dominantly inherited retinopathies.

Gene therapy - 1 Feb 2012

Farrar G J, Millington-Ward S, Chadderton N, Humphries P, Kenna P F

Abstract excerpt

In light of the elucidation of the molecular pathogenesis of some dominantly inherited retinal degenerations over the past two decades, it is timely to explore possible means of therapeutic intervention for such diseases. However, the presence of significant levels of intergenic and intragenic genetic heterogeneity in this group of dominant conditions represents a barrier to the development of therapies focused...

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Identifiers

PMID: 22089493
DOI: 10.1038/gt.2011.172

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-07.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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