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Article

Low frequency maintenance therapy with imiglucerase in adult type I Gaucher disease: a prospective randomized controlled trial.

Haematologica - 1 Feb 2007

de Fost Maaike, Aerts Johannes M F G, Groener Johanna E M, Maas Mario, Akkerman Erik M, Wiersma Maaike G, Hollak Carla E M

Abstract excerpt

BACKGROUND AND OBJECTIVES: Gaucher disease type I can be successfully treated with enzyme replacement therapy (ERT). In order to reduce the burden of the intravenously administered enzyme, a low frequency of administration was prospectively studied in patients with stable and minor disease following ERT. DESIGN AND METHODS: Eleven patients were randomly assigned either to continue their original regimen of a dose...

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PMID: 17296571
DOI: 10.3324/haematol.10635

Genes

ACE

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-08.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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