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Article

[Gene therapy for muscular dystrophy].

No to hattatsu = Brain and development - 1 Mar 2004

Takeda Shin'ichi

Abstract excerpt

Duchenne muscular dystrophy (DMD) is an X-linked, lethal muscle disorder caused by mutations in the dystrophin gene. Although an adeno-associated virus (AAV) vector-mediated gene transfer provides an attractive approach to the treatment of DMD, limitation in insertion size up to 4.9 kb excludes i...

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Share to Mice, Transgenic
Share to Muscular Dystrophy, Animal
Share to Muscular Dystrophy, Duchenne

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Share to Genetic Vectors

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Source

Identifiers

PMID: 15031985

Genes

DMD

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 1 Sept 2026. Prepared record publication-15031985-2026-09-01.1. Manifest publication-graph-cohort-2026-09-01.1.

Source receipt: PubMed via Helena Literature Corpus, retrieved 1 Sept 2026.

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[Gene therapy for muscular dystrophy].PMID 15031985Read ↗

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