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Article

Correction of the dystrophic phenotype by in vivo targeting of muscle progenitor cells.

Human gene therapy - 10 Oct 2003

Kobinger Gary P, Louboutin Jean-Pierre, Barton Elisabeth R, Sweeney H Lee, Wilson James M

Abstract excerpt

Successful gene therapy for most inherited diseases will require stable expression of the therapeutic gene. This can be addressed with integrating or self-replicating viruses by targeting postmitotic cells that have a long lifetime or stem cells that can replenish defective tissue with corrected...

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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Source

Identifiers

PMID: 14577924
DOI: 10.1089/104303403769211655

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 1 Sept 2026. Prepared record publication-14577924-2026-09-01.1. Manifest publication-graph-cohort-2026-09-01.1.

Source receipt: PubMed via Helena Literature Corpus, retrieved 1 Sept 2026.

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