Duchenne Muscular Dystrophy: Current Knowledge, Treatment, and Future Prospects

Abstract excerpt

The cloning of the dystrophin gene has led to major advances in the understanding of the molecular genetic basis of Duchenne, Becker, and other muscular dystrophies associated with mutations in genes encoding members of the dystrophin-associated glycoprotein complex. The recent introduction of pharmaceutical agents such as prednisone has shown great promise in delaying the progression of Duchenne muscular...

Topics

Share this publication in a Topic to start or enrich a Post.

• Share to Muscle Physiology and Disorders
• Share to Telomeres, Telomerase, and Senescence
• Share to Virus-based gene therapy research