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Article

Rescue of skeletal muscles of gamma-sarcoglycan-deficient mice with adeno-associated virus-mediated gene transfer.

Molecular therapy : the journal of the American Society of Gene Therapy - 1 Feb 2000

Cordier L, Hack A A, Scott M O, Barton-Davis E R, Gao G, Wilson J M, McNally E M, Sweeney H L

Abstract excerpt

In humans, a subset of cases of Limb-girdle muscular dystrophy (LGMD) arise from mutations in the genes encoding one of the sarcoglycan (alpha, beta, gamma, or delta) subunits of the dystrophin-glycoprotein complex. While adeno-associated virus (AAV) is a potential gene therapy vector for these d...

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Source

Identifiers

PMID: 10933922
DOI: 10.1006/mthe.1999.0019

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 4 Sept 2026. Prepared record publication-10933922-2026-09-04.2. Manifest publication-graph-cohort-2026-09-04.2.

Source receipt: PubMed via Helena Literature Corpus, retrieved 4 Sept 2026.

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