Article

Gene-Based Therapy for the Treatment of Spinal Muscular Atrophy Types 1 and 2 : A Systematic Review and Meta-Analysis

2023-12-07

Abstract excerpt

<title>Abstract</title> <p><bold>Background: </bold> Despite numerous studies identifying the advantages of therapies for spinal muscular atrophy (SMA), healthcare professionals encounter obstacles in determining the most effective treatment. This study aimed to investigate the effects of gene-based therapy for SMA. Objective : <bold>Methods: </bold>A systematic search was conducted from inception to November 202...

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Literature Corpus work: d8fb40ca-cbc9-58e6-9509-8ec3aa4d19af
DOI: 10.21203/rs.3.rs-3488410/v1

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