Article

Rare musculoskeletal diseases in adults: a research priority setting partnership with The James Lind Alliance

2020-04-04

Abstract excerpt

<title>Abstract</title> <p>Background: Osteogenesis imperfecta, fibrous dysplasia/McCune-Albright syndrome and X-linked hypophosphatemia are three rare musculoskeletal diseases characterised by bone deformities, frequent fractures and pain. Little high-quality research exists on appropriate treatment and long-term management of these conditions in adults. This is further worsened by limited research funding in ra...

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Literature Corpus work: b74d12e0-8318-51a6-8966-f9d870af6e64
DOI: 10.21203/rs.3.rs-20724/v1

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