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Clinical outcome of the Intrathecal administration of the allogeneic side population Adipose Derived Mesenchymal Stem Cells in Werdnig Hoffman patients: An open-label Phase I clinical trial

2020-12-08

Abstract excerpt

<h4>Background: </h4> Werdnig Hoffman (WH), a hereditary neurodegenerative disorder of lower motoneurons associated with progressive muscle weakness is the most common genetic cause of infant mortality. There is no effective treatment for WH exists. The field of translational research is active now, and clinical trials or case studies are ongoing. We present a phase 1 clinical trial in patients with WH who receive...

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Literature Corpus work
97cc805d-c4db-5010-99ca-b2e73c2824df
DOI
10.21203/rs.3.rs-122983/v1
Open publication

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Clinical outcome of the Intrathecal administration of the allogeneic side population Adipose Derived Mesenchymal Stem Cells in Werdnig Hoffman patients: An open-label Phase I clinical trialDOI 10.21203/rs.3.rs-122983/v1
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