Article

NATURAL HISTORY OF LAFORA DISEASE A Prognostic Systematic Review and Individual Participant Data Meta-Analysis

2021-06-20

Abstract excerpt

<h4>ABSTRACT</h4> <h4>Objective</h4> To describe the clinical course of Lafora Disease (LD) and identify predictors of outcome by means of a prognostic systematic review with individual participant data meta-analysis. <h4>Methods</h4> A search was conducted on MEDLINE and Embase with no restrictions on publication date. Only studies reporting genetically confirmed LD cases were included. Kaplan-Meier estimate was...

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Literature Corpus work: 4a5f58eb-9ebb-56fa-80b5-8c62049e1787
DOI: 10.1101/2021.06.17.21259096

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