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Patient, consumer and societal values, perceptions and preferences on high-cost gene therapies

2025-11-20

Abstract excerpt

<title>Abstract</title> <p>Novel cell and gene therapies hold great potential to alter the clinical course of a range of chronic diseases, yet significant uncertainties remain regarding their long-term efficacy and impact. These uncertainties pose challenges for Health Technology Assessment (HTA) committees, which systematically assess health interventions seeking public subsidy. Hematological conditions are a co...

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Literature Corpus work: 0ce400b6-b88b-548c-bb4c-5e9881f0e686
DOI: 10.21203/rs.3.rs-7872591/v1

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