Discover Community Create You

Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Gene transfer for the eventual treatment of Fanconi's anemia.

Seminars in hematology - 1 Apr 1998

Liu J M

Abstract excerpt

Aplastic anemia can be either acquired or congenital. The paradigm for the congenital form is Fanconi's anemia (FA). FA is an autosomal recessive, genetic syndrome characterized by progressive bone marrow failure, developmental abnormalities, and a predisposition to malignancy. The clinical manifestations of FA are heterogeneous, but one common outcome in the majority of patients is the development of...

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to Cell Cycle Proteins
Share to Disease Models, Animal
Share to DNA

Methodology Data sources Editorial policy Privacy Delete account & data About Contact Helena Bioinformatics

Share to DNA-Binding Proteins

Share to Nuclear Proteins

Share to Phenotype

Share to Proteins

Source

Identifiers

PMID: 9565158

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-08.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence. Graph snapshot: 2026-09-29.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Gene transfer for the eventual treatment of Fanconi's anemia.PMID 9565158Read ↗

Advances in Gene Therapy for Fanconi Anemia.Semantic proximity Read ↗

Stem Cell Gene Therapy for Fanconi Anemia: Report from the 1st International Fanconi Anemia Gene Therapy Working Group MeetingSemantic proximity Read ↗

Gene transfer to hematopoietic stem cells: implications for gene therapy of human disease.Semantic proximity Read ↗

Cell and Gene Therapy for Anemia: Hematopoietic Stem Cells and Gene EditingSemantic proximity Read ↗

The potential of gene therapy approaches for the treatment of hemoglobinopathies: achievements and challengesSemantic proximity Read ↗

Gene Therapy Through Autologous Transplantation of Gene-Modified Hematopoietic Stem CellsSemantic proximity Read ↗

How I manage patients with Fanconi anaemia.Semantic proximity Read ↗

Gene therapy for hemoglobinopathies: progress and challenges.Semantic proximity Read ↗

Gene Therapy for β-Hemoglobinopathies.Semantic proximity Read ↗

Gene therapy of Fanconi anemia: preclinical efficacy using lentiviral vectors.Semantic proximity Read ↗

Gene therapy targeting haematopoietic stem cells for inherited diseases: progress and challengesSemantic proximity Read ↗

Gene Therapy Restores the Transcriptional Program of Hematopoietic Stem Cells in Fanconi AnemiaSemantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.