Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Advances in Gene Therapy for Fanconi Anemia.

Human gene therapy - 1 Oct 2018

Río Paula, Navarro Susana, Bueren Juan A

Abstract excerpt

Fanconi anemia (FA) is a rare inherited disease that is associated with bone marrow failure and a predisposition to cancer. Previous clinical trials emphasized the difficulties that accompany the use of gene therapy to treat bone marrow failure in patients with FA. Nevertheless, the discovery of new drugs that can efficiently mobilize hematopoietic stem cells (HSCs) and the development of optimized procedures for...

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to Gene Editing
Share to Gene Transfer Techniques
Share to Genetic Therapy

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Share to Hematopoietic Stem Cells

Share to Fanconi Anemia

Share to Lentivirus

Share to Retroviridae

Share to Transduction, Genetic

Source

Identifiers

PMID: 30117331
DOI: 10.1089/hum.2018.124

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 2 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Advances in Gene Therapy for Fanconi Anemia.PMID 30117331Read ↗

Gene transfer for the eventual treatment of Fanconi's anemia.Semantic proximity Read ↗

Stem Cell Gene Therapy for Fanconi Anemia: Report from the 1st International Fanconi Anemia Gene Therapy Working Group MeetingSemantic proximity Read ↗

Gene therapy of Fanconi anemia: preclinical efficacy using lentiviral vectors.Semantic proximity Read ↗

Stem Cell Collection and Gene Transfer in Fanconi AnemiaSemantic proximity Read ↗

Functional correction of Fanconi anemia group A hematopoietic cells by retroviral gene transfer.Semantic proximity Read ↗

Engraftment of Hematopoietic Progenitor Cells Transduced with the Fanconi Anemia Group C Gene (FANCC)Semantic proximity Read ↗

Preclinical protocol for in vivo selection of hematopoietic stem cells corrected by gene therapy in Fanconi anemia group C.Semantic proximity Read ↗

[Molecular analysis and gene therapy in Fanconi anemia].Semantic proximity Read ↗

Phenotype correction of Fanconi anemia group A hematopoietic stem cells using lentiviral vector.Semantic proximity Read ↗

Gene Therapy Restores the Transcriptional Program of Hematopoietic Stem Cells in Fanconi AnemiaSemantic proximity Read ↗

Fanconi anemia: a model disease for studies on human genetics and advanced therapeutics.Semantic proximity Read ↗

In vivo selection of wild-type hematopoietic stem cells in a murine model of Fanconi anemia.Semantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.