Article
An update on Becker muscular dystrophy.
Current opinion in neurology - 1 Oct 2023
Straub Volker, Guglieri Michela
Abstract excerpt
PURPOSE OF REVIEW: The purpose of this review is to summarise the recent developments in trial readiness, natural history studies, and interventional clinical trials for Becker muscular dystrophy (BMD). RECENT FINDINGS: As several treatment concepts have claimed to convert patients with Duchenne muscular dystrophy (DMD) into a BMD phenotype, BMD itself has moved into the focus of clinical research. Natural...
Topics
- Humans
- Muscular Dystrophy, Duchenne
- Phenotype
- Research Design
