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Article

CRISPR/Cas9 gene editing therapies for cystic fibrosis

8 Jan 2021

Abstract excerpt

Introduction: Cystic fibrosis (CF) is a life-limiting genetic disorder affecting approximately 70,000 people worldwide. Current burden of treatment is high. While the latest pharmaceutical innovation has benefitted many, patients with certain genotypes remain excluded. Gene editing has the potential to correct the underlying cause of disease for all patients, representing a permanent cure.Areas covered: Various...

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CRISPR and Genetic Engineering
Cystic Fibrosis Research Advances
Pluripotent Stem Cells Research

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Identifiers

PMID: 33412935
DOI: 10.1080/14712598.2021.1869208

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