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Article

Patient-reported outcome measures in inherited retinal degeneration gene therapy trials.

Ophthalmic genetics - 1 Feb 2020

Lacy Gabrielle D, Abalem Maria Fernanda, Musch David C, Jayasundera Kanishka T

Abstract excerpt

Patient-reported outcome (PRO) measures have the potential to uniquely capture patient experience and serve as an outcome measure in inherited retinal degeneration (IRD) gene therapy trials. An IRD-specific patient-reported outcome measure may yield valuable information that has not been obtained from inherited retinal dystrophy gene therapy trials published to-date. Existing PRO measures have inherent...

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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Identifiers

PMID: 32100594
DOI: 10.1080/13816810.2020.1731836
PMCID: PMC7110960

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 6 Sept 2026. Manifest publication-graph-cohort-2026-09-06.1.

Source receipt: pubmed, retrieved 6 Sept 2026.

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