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Molecular Therapies for Choroideremia

23 Sept 2019

Abstract excerpt

Advances in molecular research have culminated in the development of novel gene-based therapies for inherited retinal diseases. We have recently witnessed several groundbreaking clinical studies that ultimately led to approval of Luxturna, the first gene therapy for an inherited retinal disease. In parallel, international research community has been engaged in conducting gene therapy trials for another more...

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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PMID: 31548516
DOI: 10.3390/genes10100738

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