Discover Community Create You

Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Repeated AAV-mediated gene transfer by serotype switching enables long-lasting therapeutic levels of hUgt1a1 enzyme in a mouse model of Crigler–Najjar Syndrome Type I

14 Aug 2017

Abstract excerpt

No abstract is available from the source.

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to Erythrocyte Function and Pathophysiology
Share to Neonatal Health and Biochemistry
Share to Virus-based gene therapy research

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Source

Identifiers

PMID: 28805798
DOI: 10.1038/gt.2017.75

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Repeated AAV-mediated gene transfer by serotype switching enables long-lasting therapeutic levels of hUgt1a1 enzyme in a mouse model of Crigler–Najjar Syndrome Type IPMID 28805798Read ↗

Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar SyndromeSemantic proximity Read ↗

A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndromeSemantic proximity Read ↗

Repeated dosing of AAV-mediated liver gene therapy in juvenile rat and mouse models of Crigler-Najjar syndrome type ISemantic proximity Read ↗

Hyperactive sleeping beauty transposase enables persistent phenotypic correction in mice and a canine model for hemophilia B.Semantic proximity Read ↗

mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapySemantic proximity Read ↗

Gene therapy for metachromatic leukodystrophySemantic proximity Read ↗

The rapidly evolving state of gene therapySemantic proximity Read ↗

Multi-year enzyme expression in patients with mucopolysaccharidosis type VI after liver-directed gene therapySemantic proximity Read ↗

AAV Serotype-1 mediates early onset of gene expression in mouse hearts and results in better therapeutic effectSemantic proximity Read ↗

AAV8 Gene Therapy Rescues the Newborn Phenotype of a Mouse Model of Crigler-Najjar.Semantic proximity Read ↗

<i>In Vivo</i> Delivery of Therapeutic Molecules by Transplantation of Genome-Edited Induced Pluripotent Stem CellsSemantic proximity Read ↗

High and long-term von Willebrand factor expression after Sleeping Beauty transposon-mediated gene therapy in a mouse model of severe von Willebrand disease.Semantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.