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Article

Antisense Oligonucleotide Therapy for Inherited Retinal Dystrophies.

Advances in experimental medicine and biology - 1 Jan 2016

Gerard Xavier, Garanto Alejandro, Rozet Jean-Michel, Collin Rob W J

Abstract excerpt

Inherited retinal dystrophies (IRDs) are an extremely heterogeneous group of genetic diseases for which currently no effective treatment strategies exist. Over the last decade, significant progress has been made utilizing gene augmentation therapy for a few genetic subtypes of IRD, although several technical challenges so far prevent a broad clinical application of this approach for other forms of IRD. Many of...

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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Identifiers

PMID: 26427454
DOI: 10.1007/978-3-319-17121-0_69

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-08.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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