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Article

Endgame: Glybera Finally Recommended for Approval as the First Gene Therapy Drug in the European Union

1 Oct 2012

Abstract excerpt

In an Editorial published earlier this year in Molecular Therapy,1Ylä-Herttuala S The need for increased clarity and transparency in the regulatory pathway for gene medicines in the European Union.Mol Ther. 2012; 20: 471-472Abstract Full Text Full Text PDF PubMed Scopus (5) Google Scholar I described the regulatory uncertainty surrounding the evaluation of Glybera (alipogene tiparvovec) by the European Medicines...

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Methodology Data sources Editorial policy Privacy Delete account & data About Contact Helena Bioinformatics

Identifiers

PMID: 23023051
DOI: 10.1038/mt.2012.194

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