Clinical application of somatic gene therapy in inborn errors of metabolism.

doi:10.1007/BF01799515

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Article

Clinical application of somatic gene therapy in inborn errors of metabolism.

Journal of inherited metabolic disease - 1 Jan 1990

Ledley F D

Abstract excerpt

Rapid advances in recombinant DNA and gene transfer technologies provide the potential for somatic gene therapy of inborn errors of metabolism in which the genetically defective function will be restored by transfer of a normal gene into somatic cells. The therapeutic potential and safety of gene...

Topics

Animals
Cloning, Molecular
DNA, Recombinant
Forecasting
Gene Expression
Genetic Therapy
Humans
Metabolism, Inborn Errors
Mutation
Organ Specificity

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