Discover Community Create You

Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Novel treatment for neuronopathic lysosomal storage diseases--cell therapy/gene therapy.

Current molecular medicine - 1 Feb 2002

Eto Yoshikatsu, Ohashi Toya

Abstract excerpt

Most lysosomal storage diseases (LSD) exhibit neurological symptoms and there has been limited success in their treatment. Innovative treatments employing novel therapy or gene therapy may offer the prospect of improvement. Recent attempts to treat the neurological forms of LSD include neural stem cell therapy, mesenchymal stem cell therapy, hematopoietic stem cell therapy and gene therapy. Additional approaches...

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to Dependovirus
Share to Enzymes
Share to Genetic Therapy

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Share to Hematopoietic Stem Cell Transplantation

Share to Lentivirus

Share to Lysosomal Storage Diseases

Share to Spleen

Source

Identifiers

PMID: 11898850
DOI: 10.2174/1566524023363112

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-07.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Novel treatment for neuronopathic lysosomal storage diseases--cell therapy/gene therapy.PMID 11898850Read ↗

Gene therapy for lysosomal storage disordersSemantic proximity Read ↗

Cell and Gene-Based Therapies for the Lysosomal Storage DiseasesSemantic proximity Read ↗

An update on gene therapy for lysosomal storage disordersSemantic proximity Read ↗

Hematopoietic Stem Cell Gene Therapy for Storage Disease: Current and New IndicationsSemantic proximity Read ↗

Gene therapy for lysosomal storage disordersSemantic proximity Read ↗

Stem Cell Therapy for the Central Nervous System in Lysosomal Storage DiseasesSemantic proximity Read ↗

New strategies for the treatment of lysosomal storage diseases (Review)Semantic proximity Read ↗

Recent advances in gene therapy for lysosomal storage disordersSemantic proximity Read ↗

Gene therapy for the neurological manifestations in lysosomal storage disordersSemantic proximity Read ↗

Treatment of lysosomal storage disorders: successes and challengesSemantic proximity Read ↗

Clinical Trials for Gene Therapy in Lysosomal Diseases With CNS InvolvementSemantic proximity Read ↗

Evolving therapies in neuronopathic LSDs: opportunities and challenges.Semantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.