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Article

Enzyme replacement treatment in type 1 and type 3 Gaucher's disease.

Lancet (London, England) - 17 Dec 1994

Bembi B, Zanatta M, Carrozzi M, Baralle F, Gornati R, Berra B, Agosti E

Abstract excerpt

The development of intravenous enzyme-replacement treatment for Gaucher's disease has changed life expectancy in cases without neurological involvement (type 1). The effects in patients with neurological involvement are unknown. We treated 12 Italian patients, types 1 (9) and 3 (3), with intravenous alglucerase: 70-120 IU/kg per month for type 3 and 30-60 IU/kg per month for type 1. Maintenance infusions were...

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Identifiers

PMID: 7996964
DOI: 10.1016/s0140-6736(94)90462-6

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-08.1.

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