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Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trials

1 Dec 2024

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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PMID: 39642902
DOI: 10.1016/s0140-6736(24)01880-4

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