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Welcoming the Era of Gene Editing in Medicine

24 Apr 2024

Abstract excerpt

Recent approvals of exa-cel for treatment of sickle cell disease and transfusion-dependent β-thalassemia mark the dawn of the era of gene editing in medicine. But ensuring access will be challenging.

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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Identifiers

PMID: 38657270
DOI: 10.1056/nejmp2314279

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