Article
Advances and Challenges in the Development of Gene Therapy Medicinal Products for Rare Diseases
1 Sept 2023
Abstract excerpt
The development of viral vectors and recombinant DNA technology since the 1960s has enabled gene therapy to become a real therapeutic option for several inherited and acquired diseases. After several ups and downs in the gene therapy field, we are currently living a new era in the history of medicine in which several ex vivo and in vivo gene therapies have reached maturity. This is testified by the recent...
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